WE ARE WORKING TO MAKE A DIFFERENCE FOR KIDS WITH SMARD1 AND CMT2S
Our mission is to find safe and effective treatments and ultimately a cure for IGHMBP2 related disorders, including SMARD1 and CMT2S.
We envision a world where individuals with rare diseases and their families are no longer told there are no medical treatments available. Our organization wants to be there to support these orphan causes, to give hope to families, and to be a leader in driving research.
Join the 200 Commit Club!!
Commit to raising $5,000 in the next 3 months. With 200 committed individuals or groups of people, we will meet our $1,000,000 goal!