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WE ARE WORKING TO MAKE A DIFFERENCE FOR KIDS WITH SMARD1 AND CMT2S
Our Mission
Our mission is to find safe and effective treatments and ultimately a cure for IGHMBP2 related disorders, including SMARD1 and CMT2S.
Our Vision
We envision a world where individuals with rare diseases and their families are no longer told there are no medical treatments available. Our organization wants to be there to support these orphan causes, to give hope to families, and to be a leader in driving research.
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